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Official patient site about a new FDA-approved sickle cell disease gene therapy option. View the treatment journey, safety and efficacy information, and clinical study results.
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5 days ago · For the eight million people across the world, including the 100,000 in the U.S., who have sickle cell disease, these gene therapies could be life-changers. Yet immediately after the approvals ...
5 days ago · Seeking a sickle cell cure: 12-year-old in DC is 1st patient in US to get new gene therapy Kendric Cromer stands a chance at becoming the first person cured of sickle cell disease with gene therapy.
3 days ago · According to the U.S. Centers For Disease Control and Prevention, approximately 100,000 people live with sickle cell disease in the U.S. Ninety percent of them are African American.
3 days ago · From The Left. Kendric Cromer, 12, is the first patient in the United States to undergo a newly approved gene therapy for sickle cell disease. Kendric is being treated at Children’s National Hospital in Washington, D.C. By next year, he may become the first person cured of sickle cell disease with gene therapy. Kendrick suffers daily ...
4 days ago · Last fall, to great fanfare, US regulators approved two gene therapies for sickle cell disease, and the European Union and UK soon followed. Many people hope that these treatments will provide a “functional cure” for the genetic condition, which causes rigid, misshapen red blood cells that lead to anemia, episodes of extreme pain, blood ...
3 days ago · Kendric Cromer, a 12-year-old with sickle cell disease (SCD) in the U.S. became the first patient to receive newly approved gene therapy treatment at Children's National Hospital in D.C. with the possibility to be cured by next year. Kendric and his family shared their experience with News4, discussing the potential impact of the treatment.
17 hours ago · The New York Times recently reported on a new gene therapy treatment for Sickle Cell Disease, which affects an estimated 100,000 people in the United States. This disease causes red blood cells to develop an abnormal “C” shape, leading to a shortage of blood cells and blockages in the circulatory system.
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related to: sickle cell disease cureSickle cell disease HCP site. Sign up to stay in the know on the latest gene therapy info. Learn about a treatment option for patients diagnosed with sickle cell disease.
Official patient site about a new FDA-approved sickle cell disease gene therapy option. View the treatment journey, safety and efficacy information, and clinical study results.
Oxbryta® (voxelotor) Tablets. Oxbryta® (voxelotor) Tablets For Oral Suspension. Browse Our Patient Resources & Caregiver Tips To Learn More.
