Search results
Dec 8, 2023 · The Food and Drug Administration on Friday approved a powerful treatment for sickle cell disease, a devastating illness that affects more than 100,000 Americans, the majority of whom are Black.
- 2 min
- Berkeley Lovelace Jr.,Marina Kopf
6 days ago · 185. Kendric Cromer, 12, the first commercial patient for Bluebird Bio’s gene therapy to cure his sickle cell disease, in the hospital as his bone marrow stem cells were being removed for...
Dec 22, 2022 · Treatment. Management of sickle cell anemia is usually aimed at avoiding pain episodes, relieving symptoms and preventing complications. Treatments might include medicines and blood transfusions. For some children and teenagers, a stem cell transplant might cure the disease.
Dec 8, 2023 · Casgevy, a cell-based gene therapy, is approved for the treatment of sickle cell disease in patients 12 years of age and older with recurrent vaso-occlusive crises. Casgevy is the first...
Dec 12, 2023 · A national, multicenter clinical trial (BMT CTN 1507) of low-dose haploidentical (half-matched) bone marrow transplant to treat severe sickle cell disease found the treatment to be safe and curative for adults with serious sickle cell-related health complications.
Apr 23, 2024 · A blood and bone marrow transplant is currently the only cure for some patients who have sickle cell disease. Medicines to treat sickle cell disease include voxelotor, hydroxyurea, crizanlizumab-tmca, L-glutamine, ibuprofen, and penicillin. Blood transfusions can also help.
Dec 8, 2023 · Gene-editing, which allows scientists to manipulate the basic building blocks of life more easily than ever before, is being studied as a treatment for illnesses ranging from rare genetic disorders...
